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Journal: ACS Chemical Neuroscience
Article Title: Polyglutamine (PolyQ) Diseases: Navigating the Landscape of Neurodegeneration
doi: 10.1021/acschemneuro.4c00184
Figure Lengend Snippet: Drugs for PolyQ diseases in commercial preclinical development
Article Snippet:
Techniques: Gene Expression, Derivative Assay, Ubiquitin Proteomics, CRISPR, shRNA, Inhibition, Functional Assay, Plasmid Preparation, Transmission Assay, Zinc-Fingers, Mutagenesis